The resubmitted BLA includes comprehensive responses to chemistry, manufacturing, and controls (CMC)-related observations outlined in a Complete Response Letter (CRL) issued in July 2025, as well as ...
PPT1 is a recombinant protein used to treat an ultra-rare disease called Batten disease CLN1 for which there is ...
When it comes to powering aircraft, jet engines need dense, energy-packed fuels. Right now, nearly all of that fuel comes ...
How big of a role do our genes play in our lifespan? Quite a bit more than previously thought, a new study suggests.
Jacobin on MSNOpinion
Silicon Valley’s latest dubious offering: designer babies
Riders of the New York City subway were startled recently by an ad campaign commissioned by a newly established reproductive ...
A new study confirms this long-held theory, discovering that 60 percent of defective genetic pairs impacting the production ...
Gene Solutions and Pangea Laboratory Establish Strategic Collaboration to Validate Laboratory Developed ctDNA Tests for Precision Screening and Cancer Care in the U.S.
No gene acts alone: interacting variants and protein partnerships can worsen, mask or even rescue disease risk, demanding ...
Explore RNA interference methods, comparing siRNA and shRNA for gene knockdown, their mechanisms, advantages, and ...
Routine newborn screening (NBS) has transformed early disease detection. However, traditional biochemical tests limit the range of conditions that can be identified at birth. Next-generation ...
New collaboration empowers customers with sequence-perfect constructs as long as 50 kb Integrated DNA Technologies (IDT), a Danaher company and a global leader in genomics, and Ansa Biotechnologies, ...
KJ Muldoon received a groundbreaking new treatment earlier this year. The baby saved from a rare disease by a first-ever personalized gene fix has reached a big milestone, taking his first steps ahead ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results